Global Gene and Cell Therapies Targeting CNS Disorders Market is expected to grow at a 30.5% CAGR during the forecast period of 2025 to 2034.
Gene and Cell Therapies Targeting CNS Disorders Market Size, Share & Trends Analysis Report By Products (Gene Therapy and Cell Therapy), By Indications, Region And Segment Forecasts, 2025 to 2034
Key Industry Insights & Findings from the Report:
Cell and gene therapy-based therapies have the potential to be an effective and disease-modifying treatment for diseases that would otherwise be incurable with traditional medicines. Due to the rising demand for cell-based immunotherapies and gene therapy products to treat conditions such as prostate and blood cancers. Another factor driving market expansion is the increasing use of cell therapy products in hospitalized patients to treat burns, venous leg ulcers, diabetic foot ulcers, traumas, and pressure ulcers. Also, due to excellent safety and efficacy profiles for treating a wide range of disorders, specific cell and gene therapy treatments are getting regulatory approvals faster than other medicines. As the approval process becomes more simplified, companies are launching these items on the market more quickly.
Additionally, rising R&D efforts, government initiatives to utilize sustainable components in manufacturing, and investments by major players are likely to generate lucrative revenue opportunities for players in the global Gene and Cell Therapies Targeting CNS Disorders Targeting CNS Disorders market over the forecast period. During the projection period, the recurrence of the current pandemic is likely to have a positive impact on the worldwide Gene and Cell Therapies Targeting CNS Disorders market. Due to the increased intervention of life-threatening diseases such as heart disease, AIDS, cystic fibrosis, and age-related problems, the industry is likely to expand its borders. The high cost of gene treatments, on the other hand, is expected to hinder market expansion to some extent throughout the forecast period.
The Gene and Cell Therapies Targeting CNS Disorders market is segmented based on product and Indication. Based on the product, the market is segmented as gene therapy and cell therapy. By Indication, the market is segmented into amyotrophic Lateral Sclerosis, Multiple sclerosis, Spinal Cord Injure, Alzheimer, Parkinson Disease, Huntington, and Other Indications. Based on Indications, the Huntington segment is accounted as a major contributor in the Gene and Cell Therapies Targeting CNS Disorders market. The Huntington category is expected to hold a major share in the global Gene and Cell Therapies Targeting CNS Disorders Targeting CNS Disorders market in 2021. As a result of the approval of an increasing number of gene therapies for cancer therapy and the segment's growth is being fueled by greater emphasis on research to develop effective cancer treatments, as well as rising cancer research investments.
The market is expected to develop in the coming years due to the availability of numerous gene therapy products that can be used to treat cancer and a huge patient population. Cell therapy segment witness growth at a rapid rate. The cell therapy segment is projected to grow at a rapid rate in the global Gene and Cell Therapies Targeting CNS Disorders Targeting CNS Disorders market. The cell therapy segment is growing due to the introduction of innovative and breakthrough products as well as the widespread use of CAR T-cell-based therapies. Cell therapy is the most rapidly developing technology in cancer treatment, with the potential to replace multiple present treatments., especially in countries such as the US, Germany, UK, China, and India.
The North America gene and cell therapy market is expected to show the highest market share in terms of revenue soon. In both regional and global markets, the United States is the major contributor. This is due to the introduction of novel cell and gene therapy products. Due to the elevated prevalence of chronic diseases in countries like China and Japan, APAC is expected to become a key market during the forecast period. Developers of cell and gene therapies are receiving support from both the public and private sectors. In terms of R&D activity and financing to develop and commercialize cell and gene therapy products, North America and Europe are at the forefront. The regulatory approval process, particularly in the United States, is evolving and becoming favourable for vendors for developing cell and gene therapy products.
| Report Attribute | Specifications |
| Growth Rate CAGR | CAGR of 30.5% from 2025 to 2034 |
| Quantitative Units | Representation of revenue in US$ Million and CAGR from 2025 to 2034 |
| Historic Year | 2021 to 2024 |
| Forecast Year | 2025-2034 |
| Report Coverage | The forecast of revenue, the position of the company, the competitive market structure, growth prospects, and trends |
| Segments Covered | By Products, By Indications |
| Regional Scope | North America; Europe; Asia Pacific; Latin America; Middle East & Africa |
| Country Scope | U.S.; Canada; U.K.; Germany; China; India; Japan; Brazil; Mexico; The UK; France; Italy; Spain; South Korea; South East Asia |
| Competitive Landscape | Novartis, Brainstorm Cell Therapeutics, Helminth, Core set, Q therapeutics, Helminth, Rapa Therapeutics, Brainstorm Cell Therapeutics, Neuroblast, Osteocyte Orchard Therapeutics plc. (UK), SIBIONO (China), Shanghai Sunway Biotech Co., Ltd. (China), bluebird bio, Inc. (US), Human Stem Cells Institute (Russia), Ange’s, Inc. (Japan), Alnylam Pharmaceuticals, Inc. (US), Sarepta Therapeutics (US), Jazz Pharmaceuticals, Inc. (Ireland), Ackee Therapeutics (US), and Donavan Technologies (US) |
| Customization Scope | Free customization report with the procurement of the report, Modifications to the regional and segment scope. Particular Geographic competitive landscape. |
| Pricing and Available Payment Methods | Explore pricing alternatives that are customized to your particular study requirements. |
Gene and Cell Therapies Targeting CNS Disorders Market , By Products-
Gene and Cell Therapies Targeting CNS Disorders Market, By Indications-
Gene and Cell Therapies Targeting CNS Disorders Market , By Region-
This study employed a multi-step, mixed-method research approach that integrates:
This approach ensures a balanced and validated understanding of both macro- and micro-level market factors influencing the market.
Secondary research for this study involved the collection, review, and analysis of publicly available and paid data sources to build the initial fact base, understand historical market behaviour, identify data gaps, and refine the hypotheses for primary research.
Secondary data for the market study was gathered from multiple credible sources, including:
These sources were used to compile historical data, market volumes/prices, industry trends, technological developments, and competitive insights.
Primary research was conducted to validate secondary data, understand real-time market dynamics, capture price points and adoption trends, and verify the assumptions used in the market modelling.
Primary interviews for this study involved:
Interviews were conducted via:
Primary insights were incorporated into demand modelling, pricing analysis, technology evaluation, and market share estimation.
All collected data were processed and normalized to ensure consistency and comparability across regions and time frames.
The data validation process included:
This ensured that the dataset used for modelling was clean, robust, and reliable.
The bottom-up approach involved aggregating segment-level data, such as:
This method was primarily used when detailed micro-level market data were available.
The top-down approach used macro-level indicators:
This approach was used for segments where granular data were limited or inconsistent.
To ensure accuracy, a triangulated hybrid model was used. This included:
This multi-angle validation yielded the final market size.
Market forecasts were developed using a combination of time-series modelling, adoption curve analysis, and driver-based forecasting tools.
Given inherent uncertainties, three scenarios were constructed:
Sensitivity testing was conducted on key variables, including pricing, demand elasticity, and regional adoption.